List of Tables
Table 1: Genetic Disorders, Common Symptoms of Genetic Disorders 14
Table 2: Genetic Disorders, Affected Areas of LSDs 15
Table 3: Genetic Disorders, Classification of Lysosomal Storage Diseases, 2017, Part 1 23
Table 4: Genetic Disorders, Classification of Lysosomal Storage Diseases, 2017, Part 2 25
Table 5: Genetic Disorders, Global, Epidemiology of Genetic Disorders, 2017 27
Table 6: Genetic Disorders, CF Severity Classification, 2017 33
Table 7: Stages of Duchenne Muscular Dystrophy, 2017 35
Table 8: Genetic Disorders, Global, CF Treatment Plan, 2017 38
Table 9: Genetic Disorders, Global, DMD Treatment Plan, 2017 39
Table 10: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Soliris, 2017 45
Table 11: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Orkambi, 2017 46
Table 12: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Cerezyme, 2017 48
Table 13: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Myozyme/Lumizyme, 2017 50
Table 14: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Fabrazyme, 2017 51
Table 15: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Pulmozyme, 2017 53
Table 16: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Kalydeco, 2017 55
Table 17: Genetic Disorders Market, Global, CFTR Gene Mutations Responsive to Kalydeco, 2017 55
Table 18: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Elaprase, 2017 57
Table 19: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Vimizim, 2017 58
Table 20: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Cerdelga, 2017 60
Table 21: Genetic Disorders Market, Global, Approved Genetic Disorders Indications for Cerdelga, 2017 61
Table 22: Genetic Disorders Market, Global, Annual Revenue Forecast for Key Products ($bn), 2016–2023 94
Table 23: Genetic Disorders Market, Global, Usage of Generics Across Key Indications, 2017 96
Table 24: Genetic Disorders Market, Global, Forecast Revenue by Company, 2016–2023 105
Table 25: Genetic Disorders Market, Global, Licensing Deals, 2006–2017 126
Table 26: Genetic Disorders Market Therapeutics Market, Global, Co-development Deals, 2006–2017 134