List of Tables
Table 1: Number of Products under Development for Thalassemia
Table 2: Number of Products under Development by Companies, Thalassemia
Table 3: Number of Products under Development by Universities/Institutes, Thalassemia
Table 4: Products under Development by Companies, Thalassemia
Table 5: Products under Development by Universities/Institutes, Thalassemia
Table 6: Number of Products under Development for Hemophilia B
Table 7: Number of Products under Development by Companies, Hemophilia B
Table 8: Number of Products under Development by Universities/Institutes, Hemophilia B
Table 9: Products under Development by Companies, Hemophilia B
Table 10: Products under Development by Universities/Institutes, Hemophilia B
Table 11: Number of Products under Development for Sickle Cell Disease
Table 12: Number of Products under Development by Companies, Sickle Cell Disease
Table 13: Number of Products under Development by Universities/Institutes, Sickle Cell Disease
Table 14: Products under Development by Companies, Sickle Cell Disease
Table 15: Products under Development by Universities/Institutes, Sickle Cell Disease
Table 16: Number of Products by Stage and Target, Thalassemia
Table 17: Number of Products by Stage and Mechanism of Action, Thalassemia
Table 18: Number of Products by Stage and Route of Administration, Thalassemia
Table 19: Number of Products by Stage and Molecule Type, Thalassemia
Table 20: Number of Products by Stage and Target, Hemophilia B
Table 21: Number of Products by Stage and Mechanism of Action, Hemophilia B
Table 22: Number of Products by Stage and Route of Administration, Hemophilia B
Table 23: Number of Products by Stage and Molecule Type, Hemophilia B
Table 24: Number of Products by Stage and Target, H2 2018, Sickle Cell Disease
Table 25: Number of Products by Stage and Mechanism of Action, Sickle Cell Disease
Table 26: Number of Products by Stage and Route of Administration, Sickle Cell Disease
Table 27: Number of Products by Stage and Molecule Type, Sickle Cell Disease
Table 28: Thalassemia – Pipeline by Acceleron Pharma Inc
Table 29: Thalassemia – Pipeline by Agios Pharmaceuticals Inc
Table 30: Thalassemia – Pipeline by bluebird bio Inc
Table 31: Thalassemia – Pipeline by Cadila Healthcare Ltd,
Table 32: Thalassemia – Pipeline by Calimmune Inc
Table 33: Thalassemia – Pipeline by CRISPR Therapeutics
Table 34: Thalassemia – Pipeline by Editas Medicine Inc
Table 35: Thalassemia – Pipeline by Errant Gene Therapeutics LLC
Table 36: Thalassemia – Pipeline by Gamida Cell Ltd
Table 37: Thalassemia – Pipeline by Gilead Sciences Inc
Table 38: Thalassemia – Pipeline by Incyte Corp
Table 39: Thalassemia – Pipeline by Ionis Pharmaceuticals Inc
Table 40: Thalassemia – Pipeline by Kiadis Pharma NV
Table 41: Thalassemia – Pipeline by La Jolla Pharmaceutical Company
Table 42: Thalassemia – Pipeline by Merck & Co Inc
Table 43: Thalassemia – Pipeline by Poseida Therapeutics Inc
Table 44: Thalassemia – Pipeline by Protagonist Therapeutics Inc
Table 45: Thalassemia – Pipeline by Sangamo Therapeutics Inc
Table 46: Thalassemia – Pipeline by Silence Therapeutics Plc
Table 47: Thalassemia – Pipeline by Vifor Pharma AG
Table 48: Hemophilia B – Pipeline by Amarna Therapeutics BV
Table 49: Hemophilia B – Pipeline by Bayer AG
Table 50: Hemophilia B – Pipeline by Bioverativ Inc
Table 51: Hemophilia B – Pipeline by Catalyst Biosciences Inc
Table 52: Hemophilia B – Pipeline by China Biologic Products Inc
Table 53: Hemophilia B – Pipeline by CSL Ltd
Table 54: Hemophilia B – Pipeline by Expression Therapeutics LLC
Table 55: Hemophilia B – Pipeline by GC Pharma
Table 56: Hemophilia B – Pipeline by Genethon SA
Table 57: Hemophilia B – Pipeline by LFB SA
Table 58: Hemophilia B – Pipeline by Logicbio Therapeutics Inc
Table 59: Hemophilia B – Pipeline by Novo Nordisk AS
Table 60: Hemophilia B – Pipeline by OPKO Biologics Ltd
Table 61: Hemophilia B – Pipeline by Pfizer Inc
Table 62: Hemophilia B – Pipeline by Pharming Group NV
Table 63: Hemophilia B – Pipeline by Promethera Biosciences SA
Table 64: Hemophilia B – Pipeline by RegenxBio Inc
Table 65: Hemophilia B – Pipeline by Sangamo Therapeutics Inc
Table 66: Hemophilia B – Pipeline by Sanofi
Table 67: Hemophilia B – Pipeline by Shire Plc
Table 68: Hemophilia B – Pipeline by Spark Therapeutics Inc
Table 69: Hemophilia B – Pipeline by UniQure NV
Table 70: Sickle Cell Disease – Pipeline by Angiocrine Bioscience Inc
Table 71: Sickle Cell Disease – Pipeline by Annexin Pharmaceuticals AB
Table 72: Sickle Cell Disease – Pipeline by ArQule Inc
Table 73: Sickle Cell Disease – Pipeline by Bio Products Laboratory Ltd
Table 74: Sickle Cell Disease – Pipeline by Bioverativ Inc
Table 75: Sickle Cell Disease – Pipeline by bluebird bio Inc
Table 76: Sickle Cell Disease – Pipeline by Bristol-Myers Squibb Co
Table 77: Sickle Cell Disease – Pipeline by Cell Source Inc
Table 78: Sickle Cell Disease – Pipeline by CRISPR Therapeutics
Table 79: Sickle Cell Disease – Pipeline by CSL Ltd
Table 80: Sickle Cell Disease – Pipeline by Editas Medicine Inc
Table 81: Sickle Cell Disease – Pipeline by Epizyme Inc
Table 82: Sickle Cell Disease – Pipeline by Errant Gene Therapeutics LLC
Table 83: Sickle Cell Disease – Pipeline by Fulcrum Therapeutics Inc
Table 84: Sickle Cell Disease – Pipeline by Gamida Cell Ltd
Table 85: Sickle Cell Disease – Pipeline by Genethon SA
Table 86: Sickle Cell Disease – Pipeline by Gilead Sciences Inc
Table 87: Sickle Cell Disease – Pipeline by Global Blood Therapeutics Inc
Table 88: Sickle Cell Disease – Pipeline by Homology Medicines, Inc
Table 89: Sickle Cell Disease – Pipeline by Incyte Corp
Table 90: Sickle Cell Disease – Pipeline by Intellia Therapeutics Inc
Table 91: Sickle Cell Disease – Pipeline by Ironwood Pharmaceuticals Inc
Table 92: Sickle Cell Disease – Pipeline by La Jolla Pharmaceutical Company
Table 93: Sickle Cell Disease – Pipeline by MaxCyte Inc
Table 94: Sickle Cell Disease – Pipeline by Merck & Co Inc
Table 95: Sickle Cell Disease – Pipeline by MimeTech Srl
Table 96: Sickle Cell Disease – Pipeline by Morphogenesis Inc
Table 97: Sickle Cell Disease – Pipeline by NKT Therapeutics Inc
Table 98: Sickle Cell Disease – Pipeline by Novartis AG
Table 99: Sickle Cell Disease – Pipeline by Orphagen Pharmaceuticals Inc
Table 100: Sickle Cell Disease – Pipeline by Oryzon Genomics SA
Table 101: Sickle Cell Disease – Pipeline by Pfizer Inc
Table 102: Sickle Cell Disease – Pipeline by Prolong Pharmaceuticals LLC
Table 103: Sickle Cell Disease – Pipeline by Protagonist Therapeutics Inc
Table 104: Sickle Cell Disease – Pipeline by ReveraGen BioPharma Inc
Table 105: Sickle Cell Disease – Pipeline by Sancilio & Company Inc
Table 106: Sickle Cell Disease – Pipeline by Sangamo Therapeutics Inc
Table 107: Sickle Cell Disease – Pipeline by Syros Pharmaceuticals Inc
Table 108: Thalassemia – Dormant Projects
Table 109: Hemophilia B – Dormant Projects
Table 110: Sickle Cell Disease – Dormant Projects
Table 111: Thalassemia – Discontinued Products
Table 112: Hemophilia B – Discontinued Products